Our science

We take great pride in conducting our clinical research to a high standard. The resulting data are shared in appropriate scientific settings and ultimately published in peer reviewed journals in a timely manner to ensure the data can credibly inform the community, as we all strive to optimise care for people with rare conditions.

In parallel with our clinical research, we invest in laboratory research to better understand how our products work and how this may relate to our clinical observations.

We fundamentally believe that the strength of scientific evidence underpins everything and how it is developed and credibly shared is the basis for our long-term success.

We place a high value on our employees having a scientific background and be a part of the conversation when it comes to advancing care.